Danish dermatology specialist Leo Pharma is paying $50 million for U.S. gene writing biotech Replay and its preclinical gene ...
A gene therapy pioneer whose invention was pivotal to a first-of-its-kind personalized gene-editing treatment for a Philadelphia-area infant is among the winners of this year’s Franklin Institute ...
The agency's decision is based on results from a clinical trial in which the treatment improved hearing in 80 percent of the ...
The treatment, developed by Regeneron Pharmaceuticals, is for a very rare form of deafness. But it represents a medical ...
Ray Therapeutics has received priority medicines (PRIME) designation from the European Medicines Agency (EMA) for its RTx-015 ...
As early results show promise, the 23-year-old hopes the treatment could finally clear a path toward his dream of becoming ...
Researchers say a gene therapy allowed deaf children and adults as old as 32 to hear for the first time. The benefits have ...
Astellas Pharma has done some spring cleaning of its pipeline, dropping two phase 1 candidates and slamming the brakes on a ...
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FDA approves first-ever gene therapy for deafness and 80 percent of kids could hear within a year
Travis used to sleep through everything. Then his mother laughed in the car and woke him up, the first time he had ever heard ...
News of the submission, which would be the first for UniQure’s closely watched treatment, comes as the therapy faces an ...
A child known publicly as Baby KJ was celebrated onstage at the twelfth Breakthrough Prize ceremony in Santa Monica last ...
New technology enables the insertion of a large segment of DNA into a genome, potentially expanding gene therapy treatment ...
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